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A Phase 3, Randomized, Double-Blind, Placebo-Controlled Efficacy and Safety Study of Ataluren in Patients with Nonsense Mutation Duchenne Muscular Dystrophy and Open-Label Extension
Treidler, Simona
(PI)
Cruz, Elizabeth
(CoPI)
Stony Brook University
Project
:
Research
Overview
Project Details
Status
Finished
Effective start/end date
08/19/19
→
06/11/21
Funding
PTC Therapeutics Inc:
$10,450.00
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