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A Phase 3, Randomized, Double-Blind, Placebo-Controlled Efficacy and Safety Study of Ataluren in Patients with Nonsense Mutation Duchenne Muscular Dystrophy and Open-Label Extension

Project: Research

Project Details

StatusFinished
Effective start/end date08/19/1906/11/21

Funding

  • PTC Therapeutics Inc: $10,450.00